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Generation and characterization of a ~F508 cystic fibrosis mouse model
Generation and characterization of a ~F508 cystic fibrosis mouse model

Characterization of two rat models of cystic fibrosis—KO and F508del  CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and  Experimental Medicine - Wiley Online Library
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library

ΔF508 - an overview | ScienceDirect Topics
ΔF508 - an overview | ScienceDirect Topics

Chemically modified hCFTR mRNAs recuperate lung function in a mouse model  of cystic fibrosis | Scientific Reports
Chemically modified hCFTR mRNAs recuperate lung function in a mouse model of cystic fibrosis | Scientific Reports

PDF) Phenotypic Characterization and Comparison of Cystic Fibrosis Rat  Models Generated Using CRISPR/Cas9 Gene Editing
PDF) Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing

Characterization of two rat models of cystic fibrosis—KO and F508del  CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and  Experimental Medicine - Wiley Online Library
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library

Generation and characterization of a ~F508 cystic fibrosis mouse model
Generation and characterization of a ~F508 cystic fibrosis mouse model

Characterization of two rat models of cystic fibrosis—KO and F508del  CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and  Experimental Medicine - Wiley Online Library
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library

Frontiers | On the Corner of Models and Cure: Gene Editing in Cystic  Fibrosis
Frontiers | On the Corner of Models and Cure: Gene Editing in Cystic Fibrosis

Characterization of two rat models of cystic fibrosis—KO and F508del  CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and  Experimental Medicine - Wiley Online Library
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library

Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models  Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect

Towards next generation therapies for cystic fibrosis: Folding, function  and pharmacology of CFTR - Journal of Cystic Fibrosis
Towards next generation therapies for cystic fibrosis: Folding, function and pharmacology of CFTR - Journal of Cystic Fibrosis

Animal models of cystic fibrosis - Journal of Cystic Fibrosis
Animal models of cystic fibrosis - Journal of Cystic Fibrosis

IJMS | Free Full-Text | Unravelling the Regions of Mutant F508del-CFTR More  Susceptible to the Action of Four Cystic Fibrosis Correctors | HTML
IJMS | Free Full-Text | Unravelling the Regions of Mutant F508del-CFTR More Susceptible to the Action of Four Cystic Fibrosis Correctors | HTML

iPSC-Derived Intestinal Organoids from Cystic Fibrosis Patients Acquire  CFTR Activity upon TALEN-Mediated Repair of the p.F508del Mutation:  Molecular Therapy - Methods & Clinical Development
iPSC-Derived Intestinal Organoids from Cystic Fibrosis Patients Acquire CFTR Activity upon TALEN-Mediated Repair of the p.F508del Mutation: Molecular Therapy - Methods & Clinical Development

Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models  Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect

In vivo correction of cystic fibrosis mediated by PNA nanoparticles |  Science Advances
In vivo correction of cystic fibrosis mediated by PNA nanoparticles | Science Advances

Frontiers | Animal Models in the Pathophysiology of Cystic Fibrosis
Frontiers | Animal Models in the Pathophysiology of Cystic Fibrosis

Rescue of ΔF508-CFTR Trafficking via a GRASP-Dependent Unconventional  Secretion Pathway: Cell
Rescue of ΔF508-CFTR Trafficking via a GRASP-Dependent Unconventional Secretion Pathway: Cell

Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models  Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect

Generation and characterization of a ~F508 cystic fibrosis mouse model
Generation and characterization of a ~F508 cystic fibrosis mouse model

Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models  Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect